Neurogene Shares NGN-401 Preclinical Data at ESGCT
Neurogene presented preclinical data for NGN-401 in Rett syndrome, discussing rapid ssAAV expression, limitations of miRNA-based auto-regulation and support for ICV delivery used in its trials.
Neurogene presented preclinical data for NGN-401 in Rett syndrome, discussing rapid ssAAV expression, limitations of miRNA-based auto-regulation and support for ICV delivery used in its trials.