ZVRA: Publishes Positive MIPLYFFA Data
Zevra Therapeutics announces publication of positive MIPLYFFA data from pediatric substudy in infants with Niemann-Pick Disease Type C
ZVRA - Zevra Therapeutics Announces Publication of Positive MIPLYFFA® Data from Pediatric Substudy in Infants with Niemann-Pick Disease Type C (NPC)Data published in Molecular Genetics and Metabolism Reports suggest MIPLYFFA (arimoclomol) was well tolerated in pediatric patients with no new safety signals observed