SQUAWK/NEWS
Account
Theme
Account
Menu
Live News REGULATION ARTICLE M impact

FDA approves ZANVASTRO for Alexander disease, broad access label

ZANVASTRO received early FDA approval as the first disease-modifying therapy for Alexander disease, with a broad label for children and adults. The pivotal trial reported motor function stabilization and a favorable safety profile.

IONS

ZANVASTRO received early FDA approval as the first disease-modifying therapy for Alexander disease, with a broad label for children and adults.

The pivotal trial showed significant motor function stabilization and a favorable safety profile.

Launch efforts focus on patient access, support programs…