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FDA approves ZANVASTRO as first disease-modifying therapy for Alexander disease

ZANVASTRO (zilganersen) is now FDA-approved as the first disease-modifying therapy for Alexander disease in both children and adults, citing pivotal trial data showing motor function stabilization and a favorable safety profile.

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ZANVASTRO (zilganersen) is now FDA-approved as the first disease-modifying therapy for Alexander disease in both children and adults, supported by pivotal trial data showing significant motor function stabilization and a favorable safety profile.

Launch strategies focus on patient transition, acces…