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RARE shares plunge after Angelman late-stage trial failure, downgraded

Ultragenyx Pharmaceutical’s experimental Angelman syndrome therapy failed a key late-stage trial, triggering analyst downgrades and fresh concerns. RARE shares were down 45% in pre-market trading.

RARE

Ultragenyx Pharmaceutical (RARE) was in focus on Thursday after its experimental Angelman syndrome therapy failed a key late-stage trial, triggering analyst downgrades and renewed concern over the company’s growth outlook. RARE shares were down 45% in pre-market trading and are on track for their biggest single-day percentage decline on record.

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